GEMMABio Announces First Patient Dosed in CHARISMA Trial of GB221, Investigational Next‑Generation Gene Therapy for Spinal Muscular Atrophy Type 1 (SMA1)
-U.S. FDA grants GB221 rare pediatric disease designation PHILADELPHIA, Feb. 26, 2026 /PRNewswire/ — Gemma Biotherapeutics (“GEMMABio”), a…