New OpenABE gene editor improves editing efficiency by up to 36 times
A joint research team led by Professor Daesik Kim (Department of Medicine, Sungkyunkwan University), along with Professor Yong-Sub…
Regeneron (REGN) Says EMA Accepted Review for Otarmeni Application
Regeneron Pharmaceuticals, Inc. (NASDAQ:REGN) is one of the 10 Best Debt-Free S&P 500 Stocks to Buy Now. On…
A mother’s 20-year quest fuels a startling Duchenne breakthrough
A year after the worst day of her life, Debra Miller received a voicemail she couldn’t quite make…
Base editing corrects genetic mutation responsible for severe form of inherited epilepsy
University of Virginia School of Medicine scientists have used a next-generation form of gene editing to fix the…
AskBio Announces FDA Acceptance of Investigational New Drug (IND) Application for AB-1009 Gene Therapy for Treatment of Late-Onset Pompe Disease (LOPD)
Durham, N.C., Jan. 08, 2026 (GLOBE NEWSWIRE) — AB-1009 program advances to Phase 1/Phase 2; clinical trial initiated…
7 medical breakthroughs of 2025
For most diseases, the challenge is not a lack of effort but the limits of existing tools and…
the events to watch for in the coming year
India’s Aditya-L1 spacecraft launched in 2023. Next year, it will observe the Sun during its peak activity phase.Credit:…
Harnessing artificial intelligence to advance CRISPR-based genome editing technologies
Zheng, Y. et al. Precise genome-editing in human diseases: mechanisms, strategies and applications. Signal. Transduct. Target. Ther. 9,…
New gene-editing method can correct many disease-causing mutations in mammalian cells
Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…
Experimental gene therapy successfully treats dozens of children with rare fatal disorder
ADVERTISEMENT An experimental gene therapy has successfully treated dozens of children with a rare and fatal immune disorder,…
Harnessing “DNA surgery” to develop therapeutic medicines for genetic liver and heart diseases
Genome editing is increasingly recognzed as a leading frontier in biomedical research and an essential driver of healthcare…
Next-generation gene therapy tools built by UH scientist
Reading time: 2 minutesAssistant Professor Jesse Owens using a program to model the structure of his integrase protein.…