Advances in chemistry and delivery are taking oligonucleotide medicines beyond rare diseases
Decades of work on RNA targeting, chemical modification, and tissue-specific delivery are reshaping what programmable genetic medicines can…
Prednisone may impair bone health in children with Duchenne muscular dystrophy
In a new study published in Scientific Reports, an international and multidisciplinary research team including Binghamton University researchers identified…
This one protein prevents muscle from turning to fats |
Human biology is not just surprising, but at the same time it is ever-evolving; a recent study has…
Sarepta Announces FDA’s Approval of Updated ELEVIDYS Prescribing Information
CAMBRIDGE, Mass., November 14, 2025–(BUSINESS WIRE)–Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases,…