gene therapy

Durham, N.C., Jan. 08, 2026 (GLOBE NEWSWIRE) — AB-1009 program advances to Phase 1/Phase 2; clinical trial initiated…

For most diseases, the challenge is not a lack of effort but the limits of existing tools and…

Science in 2026: what to expect this year NatureWhat to expect from 2026 in science, arts, politics and society The…

India’s Aditya-L1 spacecraft launched in 2023. Next year, it will observe the Sun during its peak activity phase.Credit:…

General Control enters Novo Nordisk’s Co-Creation Greenhouse to advance multiplex epigenetic editing for complex chronic disease. General Control,…

Altering a single gene may help people lower dangerously high levels of cholesterol and other fats in the…

“These findings highlight the potential of self-complementary AAVs to reduce dose requirements, minimize toxicity, and broaden clinical use…

Up to 60% of congenital and early-onset hearing loss is caused by genetic mutations in an inherited gene,…

Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…

ADVERTISEMENT An experimental gene therapy has successfully treated dozens of children with a rare and fatal immune disorder,…

In a preclinical study, UC Davis Comprehensive Cancer Center scientists developed a highly targeted gene therapy that could…

Genome editing is increasingly recognzed as a leading frontier in biomedical research and an essential driver of healthcare…

AskBio Announces FDA Acceptance of Investigational New Drug (IND) Application for AB-1009 Gene Therapy for Treatment of Late-Onset Pompe Disease (LOPD)