Keralam govt to provide lifelong SMA medication to all eligible children | Thiruvananthapuram News
Keralam health minister K Muraleedharan Thiruvananthapuram: The state govt has initiated steps to ensure lifelong access to life-saving…
CM defends health task force, generic SMA drug | Thiruvananthapuram News
Chief minister V D Satheesan Thiruvananthapuram: Chief minister V D Satheesan defended the state govt’s health task force…
SAT Hosp head defends Indian-made SMA drug, rejects trial claims | Thiruvananthapuram News
Representational AI-image Thiruvananthapuram: SAT Hospital superintendent Dr R S Riyas has urged the public not to spread misinformation…
Newborns in England now being tested for SMA after Jesy Nelson campaign
Newborn babies in England will be tested for the rare genetic condition spinal muscular atrophy (SMA) from Thursday.…
Roche cans muscle-preserving obesity drug, hands it back to Chugai
Roche has scrapped development of a muscle-building drug, ending a trial testing the experimental medicine in combination with…
Advances in chemistry and delivery are taking oligonucleotide medicines beyond rare diseases
Decades of work on RNA targeting, chemical modification, and tissue-specific delivery are reshaping what programmable genetic medicines can…
5 early signs of SMA for parents to look out for – The Irish News
Two life-changing treatments have been given the green light for routine NHS use, offering renewed hope to hundreds…
Jesy Nelson ‘bittersweet’ after Scotland becomes first to screen babies for SMA
Former Little Mix singer Jesy Nelson has said she feels “bittersweet” after Scotland became the first part of…
Scotland becomes first part of UK to screen babies for rare muscle disease – The Irish News
Scotland has become the first part of the UK to screen babies for a rare condition that causes…
Scotland becomes first part of UK to screen babies for rare muscle disease
Scotland has become the first part of the UK to screen babies for a rare condition that causes…
Zebrafish can play a decisive role in clinical interpretation of spinal muscular atrophy
The tiny zebrafish is helping researchers rapidly determine whether a newborn’s genetic mutation is likely to cause spinal…
Singer Jesy Nelson says her twins may never walk after being diagnosed with rare condition – The Journal
Singer Jesy Nelson says her twins may never walk after being diagnosed with rare condition The JournalJesy Nelson says…