Insmed’s ‘ginormous’ lung drug sales; J&J’s US pricing deal
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Flu wave’s hidden cost on people with cystic fibrosis
People with cystic fibrosis (CF) are uniquely vulnerable to the flu wave currently ripping through the UK, a…
Enterprise Therapeutics publishes results of Phase 1 study of ETD001, a novel inhaled ENaC blocker for treatment of Cystic Fibrosis, in The Journal of Cystic Fibrosis
Enterprise Therapeutics Ltd (Enterprise), a biopharmaceutical company dedicated to the discovery and development of novel therapies to improve…
New biofilm discovery may pave way to undermining antibiotic-resistant Pseudomonas
The bacterium known as Pseudomonas aeruginosa is an unwelcome visitor in the human body. Serious infections can result…
New gene-editing method can correct many disease-causing mutations in mammalian cells
Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…
Genetic investigation of sinopulmonary diseases in Vietnam: seeking specific causes from non-specific symptoms | Orphanet Journal of Rare Diseases
O’Donnell AE. Bronchiectasis – a clinical review. N Engl J Med. 2022;387(6):533–45. Article PubMed Google Scholar Flume PA,…
More families raising children with cystic fibrosis staying in the bush
Connie Lacey, 4, and Sienna Machin, 10, are like sisters, but they are not allowed to be near…
Pacbio’s Puretarget simplifies carrier screening
Up to 71% of people carry at least one pathogenic variant that could contribute to development of a…