Sickle cell gene therapies offer new hope, accessing them is hard
This microscope photo provided on Oct. 25, 2023, by the Centers for Disease Control and Prevention shows crescent-shaped…
For final 10% of cystic fibrosis patients, breakthrough hasn’t come
Emily Kramer-Golinkoff founded Emily’s Entourage in 2011 to speed up research for the final 10% of CF patients.…
A Loophole Brings Cystic Fibrosis Patients a ‘Miracle Drug’ in Generic Form
Josua Lottering stepped out the airport doors in the Bangladesh capital, Dhaka, and doubled over in coughing spasms.…
Vertex kidney drug povetacicept succeeds in trial for IgAN
A sign hangs in front of the world headquarters of Vertex Pharmaceuticals in Boston. Brian Snyder | Reuters…