FDA questions the efficacy of Capricor’s Duchenne drug
The Food and Drug Administration said Monday that Capricor Therapeutics’ stem cell treatment for Duchenne muscular dystrophy did…
Actor Lee Dong-gun Diagnosed with Rare Ankylosing Spondylitis Affecting 1% of South Koreans – 조선일보
Actor Lee Dong-gun Diagnosed with Rare Ankylosing Spondylitis Affecting 1% of South Koreans 조선일보Lee Dong-gun’s Rare Disease Struggles Shock…
Phase 3 Trial Confirms Sarilumab Improves Polymyalgia Rheumatica Outcomes
Vibeke Strand, MD Credit: PRIME Education New phase 3 data supported the effectiveness of sarilumab 200 mg every…
Patient dies in Sarepta gene therapy trial, adding to safety concerns
A 51-year-old man died last month after receiving an experimental gene therapy developed by Sarepta Therapeutics for an…