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Browsing Tag

BioMarin Pharmaceutical Inc.

2 posts
HHealthcare
BioMarin to Acquire Alesta Therapeutics to Gain ALE1, a Potential First Oral Therapy for Hypophosphatasia, Adding an Important Clinical Program to BioMarin's Pipeline
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BioMarin to Acquire Alesta Therapeutics to Gain ALE1, a Potential First Oral Therapy for Hypophosphatasia, Adding an Important Clinical Program to BioMarin’s Pipeline

  • August 18, 2026
BioMarin to pay $275 million upfront, plus additional payments upon achievement of development and regulatory milestones Alesta to…
MMedication
U.S. Food and Drug Administration Accepts BioMarin's Supplemental New Drug Application for Full Approval of VOXZOGO® (vosoritide) for Children With Achondroplasia
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U.S. Food and Drug Administration Accepts BioMarin’s Supplemental New Drug Application for Full Approval of VOXZOGO® (vosoritide) for Children With Achondroplasia

  • July 13, 2026
Application based on long-term safety and efficacy data from three ongoing studies, including adult height and additional clinical…
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