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Browsing Tag

experimental drug use

1 post
GGenetics
8-year-old wheelchair-user walks again after receiving experimental drug for rare and fatal genetic condition
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8-year-old wheelchair-user walks again after receiving experimental drug for rare and fatal genetic condition

  • July 19, 2025
An 8-year-old boy, wheelchair-bound due to a rare genetic disease, HPDL deficiency, regained his mobility through an experimental…
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