New gene-editing method can correct many disease-causing mutations in mammalian cells
Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…
Experimental gene therapy successfully treats dozens of children with rare fatal disorder
ADVERTISEMENT An experimental gene therapy has successfully treated dozens of children with a rare and fatal immune disorder,…
Harnessing “DNA surgery” to develop therapeutic medicines for genetic liver and heart diseases
Genome editing is increasingly recognzed as a leading frontier in biomedical research and an essential driver of healthcare…
Next-generation gene therapy tools built by UH scientist
Reading time: 2 minutesAssistant Professor Jesse Owens using a program to model the structure of his integrase protein.…
Huntington’s disease treated for first time using gene therapy
A brain scan of a person with Huntington’s disease, which causes a loss of brain volume as neurons…
Gene Therapy Tackles Huntington’s Progress in Landmark Trial. “This Changes Everything”
A complex genetic procedure offers new hope in the fight against one of the world’s cruellest diseases. The…
Breakthrough reveals how viruses efficiently pack genetic material
Researchers at San Diego State University and Michigan State University are shedding new light on how viruses meticulously…
ChronODE method offers precision in timing gene therapy treatments
A Yale research team has created a new computer tool that can pinpoint when exactly genes turn on…
New generation of CRISPR shows safer path to treating genetic diseases
A new generation of CRISPR technology developed at UNSW Sydney offers a safer path to treating genetic diseases…
Join Sept. 18 with George Church and this year’s top biotech startups
I asked AI the other day how many biotechs have been co-founded by Harvard’s George Church. About 50…
Prime editing corrects a childhood genetic disease in mice
Alternating hemiplegia of childhood (AHC) is a rare, one-in-a-million genetic disease that affects kids. Most cases are…
Breakthrough gene therapy reverses genetic deafness across age groups
Using gene therapy to treat hereditary deafness is safe and effective in both children and adults, according to…