In a world-first procedure, The Zayed Centre for Research into Rare Disease in Children at Great Ormond Street Hospital in London has delivered a genetic treatment for chronic granulomatous disease.
This disease is a rare disorder in which white blood cells — which fight infections — do not work as they should. These leaves the body vulnerable to bacterial and fungal infections, drastically reducing the patient’s quality of life.
However, one 19-year-old at Great Ormond Street Hospital will now have a better life thanks to the Zayed Centre. The treatment that was provided to him is a part of a world-first trial for chronic granulomatous disease. It was developed, manufactured and delivered at the hospital.
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The teenage patient will now have much better health in general, since the genetic treatment administered provides long-term stability and healthy immune cells for life.
There are further plans to use this treatment to help four other patients in the future.
A Great Ormond Street Hospital (GOSH), University College London and GOSH Charity partnership, the Zayed Centre for Research was made possible by a £60 million gift from Sheikha Fatima bint Mubarak.
