A UPMC doctor waited years for a needed drug to get approval. The FDA finally gave it – Pittsburgh Post-Gazette

A UPMC doctor waited years for a needed drug to get approval. The FDA finally gave it  Pittsburgh Post-GazetteFDA greenlights Stealth Bio’s injection as 1st treatment for Barth syndrome  Fierce PharmaFDA gives approval for treatment of rare disease affecting Hall Co. family  AccessWdunUS FDA approves first treatment for rare, life-threatening disease in males  ReutersStealth Wins Expedited FDA Nod for First-Ever Barth Syndrome Treatment  BioSpace