Insmed’s ‘ginormous’ lung drug sales; J&J’s US pricing deal
This story was originally published on BioPharma Dive. To receive daily news and insights, subscribe to our free…
New gene-editing method can correct many disease-causing mutations in mammalian cells
Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…
Genetic investigation of sinopulmonary diseases in Vietnam: seeking specific causes from non-specific symptoms | Orphanet Journal of Rare Diseases
O’Donnell AE. Bronchiectasis – a clinical review. N Engl J Med. 2022;387(6):533–45. Article PubMed Google Scholar Flume PA,…
CVS, Walgreens require prescriptions for COVID vaccines in Colorado
People who want to get an updated COVID-19 vaccine at CVS or Walgreens pharmacies in Colorado this fall…
Rescued by fat bubbles: Scientists treat rare genetic disease with designer molecule | Lifestyle
Tiny fat bubbles carrying gene therapy have successfully repaired DNA in the lungs and liver of animals with…