This British Open amateur is a qualified mechanic with cystic fibrosis and is proving an inspiration
SOUTHPORT, England (AP) — David Howard was aged 7 when he was diagnosed with cystic fibrosis. By the…
Colorado can’t cap price of arthritis drug Enbrel, judge rules
Colorado can’t cap the price of arthritis medication Enbrel while a lawsuit challenging the state’s drug affordability board’s…
Vertex makes $10B deal for commercial endocrinology biotech Crinetics – Endpoints News
Vertex makes $10B deal for commercial endocrinology biotech Crinetics Endpoints NewsVertex Pharmaceuticals to Acquire Crinetics Pharmaceuticals for $10 Billion WSJCRNX…
Cystic Fibrosis Took My Sister. I’m Living Life Fully For Her.
“What matters is how we live and love and how we spend our dash.” — Linda Ellis I…
Colorado receives FDA permission to import drugs from Canada
Colorado finally has federal permission to start importing cheaper prescription drugs from Canada, but the state may not…
UChicago Medicine performs rare quadruple organ transplant
It took some time for Jasmine Jones to absorb the news that doctors wanted to replace four of…
Insmed’s ‘ginormous’ lung drug sales; J&J’s US pricing deal
This story was originally published on BioPharma Dive. To receive daily news and insights, subscribe to our free…
New gene-editing method can correct many disease-causing mutations in mammalian cells
Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…
Genetic investigation of sinopulmonary diseases in Vietnam: seeking specific causes from non-specific symptoms | Orphanet Journal of Rare Diseases
O’Donnell AE. Bronchiectasis – a clinical review. N Engl J Med. 2022;387(6):533–45. Article PubMed Google Scholar Flume PA,…
CVS, Walgreens require prescriptions for COVID vaccines in Colorado
People who want to get an updated COVID-19 vaccine at CVS or Walgreens pharmacies in Colorado this fall…
Rescued by fat bubbles: Scientists treat rare genetic disease with designer molecule | Lifestyle
Tiny fat bubbles carrying gene therapy have successfully repaired DNA in the lungs and liver of animals with…