Gene Therapy

Exclusive: In major test for longevity field, FDA greenlights study on a ‘near total reset’ of cells Endpoints NewsScientists…

At a Food and Drug Administration cell and gene therapy (CGT) roundtable last June, most speakers pushed for…

Science in 2026: what to expect this year NatureAll the eclipses, supermoons, meteor showers and planets to spot in…

Gene therapy researchers were converging on a holy grail. A few years ago, researchers at labs and companies…

On a video call in early September, Sarah Tabrizi first saw the data that she and other researchers…

You have full access to this article via your institution. To the research team working to save him,…

A California boy is defying bleak odds after becoming the first patient to receive a new gene…

A California toddler is the first person in the world to receive gene therapy to treat his devastating…

Crystalline forms of cholesterol (blue) in a liver cell (purple), imaged using a scanning electron microscope.Credit: Steve Gschmeissner/Science…

A CRISPR-based gene editing therapy dramatically reduced levels of low-density lipoprotein, often called “bad cholesterol,” and triglycerides in…

uniQure (NASDAQ: QURE) on Nov. 3, 2025 announced FDA feedback…

Exclusive: In major test for longevity field, FDA greenlights study on a 'near total reset' of cells – Endpoints News