U.S. Cell And Gene Therapy Clinical Trials Market Trends
Dublin, Oct. 03, 2025 (GLOBE NEWSWIRE) — The “U.S. Cell And Gene Therapy Clinical Trials Market Size, Share…
A clinical milestone for CRISPR in sickle-cell disease
The haemoglobinopathies transfusion-dependent β-thalassemia (TDT) and sickle-cell disease (SCD) are two globally prevalent and severe monogenic blood disorders.…
Next-generation gene therapy tools built by UH scientist
Reading time: 2 minutesAssistant Professor Jesse Owens using a program to model the structure of his integrase protein.…
Huntington’s disease treated for first time using gene therapy
A brain scan of a person with Huntington’s disease, which causes a loss of brain volume as neurons…
New gene therapy for Huntington’s ‘changes everything’, say researchers
UK researchers say they have slowed the progression of the fatal neural condition Huntington’s disease for the first…
U.S. Cell & Gene Therapy Contract Research Organizations
Dublin, Sept. 18, 2025 (GLOBE NEWSWIRE) — The “U.S. Cell & Gene Therapy Contract Research Organizations Market Size,…
The Medicine Maker | Combatting Deafness with Gene Therapy
A study from researchers at Tel Aviv University reports that restoring a single protein…
Diversity challenges and reconciles genetics in facioscapulohumeral muscular dystrophy
Wang LH, Tawil R. Facioscapulohumeral dystrophy. Curr Neurol Neurosci Rep. 2016;16:66. Article PubMed Google Scholar Mul K, Lassche…
The genetic answer to rare diseases
The standard treatment is a liver transplant, but this entails a high risk of complications in infants. Thanks…
Personalized Medicine (Biologics, Small Molecules, Gene
Dublin, Sept. 08, 2025 (GLOBE NEWSWIRE) — The “Personalized Medicine: Market Share, and Growth Analysis by Product Type…
Molecular genetics and therapeutic development for GNE myopathy
Yoshioka W, Noguchi S, Mori-Yoshimura M, Nishino I. Advances in understanding of the natural history, mechanism, extra-muscular manifestations…
UH receives $1M grant to advance Usher Syndrome research
The University of Houston has received a two-year, $1.1 million gift from the Cynthia and George Mitchell Foundation…