For final 10% of cystic fibrosis patients, breakthrough hasn’t come
Emily Kramer-Golinkoff founded Emily’s Entourage in 2011 to speed up research for the final 10% of CF patients.…
One drug, many rare diseases
Ron Nickel | Design Pics | Getty Images CNBC Advisory Board member Dr. Anna Greka has built her…
IonQ shares rise after major quantum computing breakthrough
Shares of IonQ rose Wednesday after the company said it demonstrated the quantum computing industry’s first end-to-end real-time…
Athletes with autism take center court at the US Open
The USTA unveils the largest single investment in U.S. Open history. USTA CNBC Cures is proudly underwritten by…
Rare disease is taking his sight. Access to a treatment is hard to get
Judy and Courtney Stecker with their sons, Read (left) and Wheeler (right). Judy and Courtney Stecker CNBC Cures…
BioCryst is profitable. Now it wants to buy more rare disease drugs
CNBC Cures is proudly underwritten by Alexion, AstraZeneca Rare Disease, whose support enables our journalism to elevate stories…
FDA approves Gilead HIV pill Bixlenvo designed to simplify treatment
Gilead Bixlenvo drug Courtesy: Gilead The Food and Drug Administration approved a once-daily HIV pill from Gilead that…
The startup using AI to help build custom treatments for rare diseases
Jacalyn Lee, founder of The DAND Alliance, and her youngest daughter Isla. Jacalyn Lee CNBC Cures is proudly…
AstraZeneca and Bristol Myers Squibb mull $400 billion deal: Report
A smart acquisition strategy has made Bristol-Meyers, which has bought seven companies since October 2007, a big player…
New Medicaid work rules could leave rare disease patients uninsured
CNBC Cures is proudly underwritten by Alexion, AstraZeneca Rare Disease, whose support enables our journalism to elevate stories…
AstraZeneca stock dives 9% after heart drug trial misses target
Shares of AstraZeneca fell as much as 9% after a late-stage clinical trial for a heart disease failed…
Weight loss drug maker stock sinks 25% as safety data spooks investors
Shares of weight loss drug maker Zealand Pharma plummeted as much as 26% on Monday after new data…