Blood Cancer United buys drug stockpile for compassionate use
In a rare move, nonprofit organization Blood Cancer United announced Thursday it was buying the remaining supplies of…
Man Can’t Work Because He Gets Drunk Without Drinking
For years, Eric Poulin kept being told he had a drinking problem—while insisting he hadn’t touched a…
Scientists identify hundreds of ancient genes associated with human diseases
When a child develops kidney failure or a rare bone disorder, the cause can seem painfully immediate. It…
Carrie Ann Inaba details decade-long battle with Sjogren’s disease
NEWYou can now listen to Fox News articles! Longtime “Dancing with the Stars” judge Carrie Ann Inaba is…
FDA, urged to avoid controversy, creates new headache with attack on UniQure
Adam Feuerstein is a senior writer and biotech columnist, reporting on the crossroads of drug development, business, Wall…
FDA rejects Regenxbio’s MPS II rare-disease gene therapy
Adam Feuerstein is a senior writer and biotech columnist, reporting on the crossroads of drug development, business, Wall…
Couple donates $11 million to Lurie Children’s Hospital
A couple with deep ties to the Chicago area is donating $11 million to Lurie Children’s Hospital in…
Pharma sounds alarm over EU plans to procure novel medicines – POLITICO
But the pharmaceutical industry argues that any changes should be made cautiously and with clear guidelines for everyone…
GeneDx to Partner with Florida’s Sunshine Genetics Network, Launching Nation’s First State-Backed Genomic Newborn Screening Program
Florida Institute for Pediatric Rare Diseases and Representative Adam Anderson ushering in a new era of preventative care…
NLRP3 inflammasome and hearing loss: from mechanisms to therapies | Journal of Neuroinflammation
Sensorineural hearing loss (SNHL) affects approximately 1.5 billion people globally. Approximately 430 million of these patients require rehabilitation…
Knowing patient’s genetic make-up may change the way medicines are prescribed
SINGAPORE – Not all medicines work the same way on every patient, and part of the answer lies…
Acadia Pharmaceuticals drug for rare genetic condition fails late-stage study
Adam Feuerstein is a senior writer and biotech columnist, reporting on the crossroads of drug development, business, Wall…