{"id":350182,"date":"2025-12-15T14:09:15","date_gmt":"2025-12-15T14:09:15","guid":{"rendered":"https:\/\/www.newsbeep.com\/us\/350182\/"},"modified":"2025-12-15T14:09:15","modified_gmt":"2025-12-15T14:09:15","slug":"gene-therapy-trial-death-unnerves-promising-area-of-brain-research","status":"publish","type":"post","link":"https:\/\/www.newsbeep.com\/us\/350182\/","title":{"rendered":"Gene therapy trial death unnerves promising area of brain research"},"content":{"rendered":"

Gene therapy researchers were converging on a holy grail. A few years ago, researchers at labs and companies reported they had engineered viruses that could ferry corrective genes deep into the brain, giving potential entry to a new world of treatments for Alzheimer\u2019s, Parkinson\u2019s, and a slew of rare genetic diseases.<\/p>\n

This summer, after years of careful study, the first person underwent gene therapy using one of the new viruses. The patient, a young child, died two and a half days later.<\/p>\n

The death has sent concern and uncertainty rippling through labs and companies developing gene therapies for the brain, along with rare disease groups who hoped these tools could deliver long-sought cures. They worry that Capsida Biotherapeutics unearthed a broader risk for other viruses designed to travel like a messenger pigeon to our brains, one that could derail years of progress.\u00a0<\/p>\n

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