Using DNA sequencing for accurate identification of microbial infections in cystic fibrosis patients
Lung infections are a constant risk for people living with cystic fibrosis (CF), a life-threatening genetic disorder which…
Colorado can’t cap price of arthritis drug Enbrel, judge rules
Colorado can’t cap the price of arthritis medication Enbrel while a lawsuit challenging the state’s drug affordability board’s…
‘Lung atlas’ maps changes to immune cells of kids with cystic fibrosis
Within 24 hours of being born, Lewis Milne needed emergency surgery to remove a blockage in his small…
SA scientist creates virus weapons against antibiotic resistance
From the smallest organisms on Earth may come some of the biggest breakthroughs in science. That belief sits…
Boy, 6, takes up boxing to fight cystic fibrosis
A six-year-old boy with cystic fibrosis has taken up boxing to fight the effects of his genetic condition.…
Advancing Gene Therapy for Cystic Fibrosis
Original story from University of California, Los Angeles (UCLA; CA, USA). UCLA researchers have developed a lipid nanoparticle-based…
Updated newborn screening guidelines aim to improve cystic fibrosis detection
An updated report on cystic fibrosis (CF) from Ann & Robert H. Lurie Children’s Hospital of Chicago, in…
Insmed’s ‘ginormous’ lung drug sales; J&J’s US pricing deal
This story was originally published on BioPharma Dive. To receive daily news and insights, subscribe to our free…
Enterprise Therapeutics publishes results of Phase 1 study of ETD001, a novel inhaled ENaC blocker for treatment of Cystic Fibrosis, in The Journal of Cystic Fibrosis
Enterprise Therapeutics Ltd (Enterprise), a biopharmaceutical company dedicated to the discovery and development of novel therapies to improve…
Cystic fibrosis patients on triple-drug therapy can safely reduce daily lung treatments
A new multi-site study led by researchers at CU Anschutz shows that people with cystic fibrosis (CF) who…
New gene-editing method can correct many disease-causing mutations in mammalian cells
Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…
Genetic investigation of sinopulmonary diseases in Vietnam: seeking specific causes from non-specific symptoms | Orphanet Journal of Rare Diseases
O’Donnell AE. Bronchiectasis – a clinical review. N Engl J Med. 2022;387(6):533–45. Article PubMed Google Scholar Flume PA,…