Boy with Rare Genetic Disorder Amazes Doctors After World-First Gene Therapy
Courtesy of Oliver Chu family The first child in history has successfully been treated with a new genetic…
UPDATE Long-Term Follow-up in Babies Born with ‘Bubble Boy Disease’ Still Seem Cured
6 of the children treated for SCID living their best lives – credit, UCLA, supplied by the parents…
Massapequa couple seeks cure for daughter with rare genetic mutation
Madeline Norton was diagnosed with a rare genetic mutation, causing her family to change their outlook on life.…